ID

45686

Descripción

Principal Investigator: Helen Su, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD, USA MeSH: Immunologic Deficiency Syndromes,Epstein-Barr Virus Infections https://www.ncbi.nlm.nih.gov/projects/gap/cgi-bin/study.cgi?study_id=phs001245 We describe four patients from two unrelated families of different ethnicities who had primary immunodeficiency predominantly manifesting as susceptibility to EBV-related diseases. We performed whole exome sequencing (P1 and P2 from family 1) or whole genome sequencing (P4 and both parents from family 2) in those two families and identified homozygous frameshift or in-frame deletions in CD70 in these patients which abolished either CD70 surface expression or binding to its counter structure CD27. Sanger sequencing identified the same homozygous *CD70* mutation in P3, which is not included in the dbGaP submission. Autosomal recessive CD70 deficiency is a novel cause of combined immunodeficiency and EBV-associated diseases, reminiscent of CD27 deficiency.

Link

dbGaP study = phs001245

Palabras clave

  1. 02/05/2023 02/05/2023 - Simon Heim
Titular de derechos de autor

Helen Su, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD, USA

Subido en

2 de maio de 2023

DOI

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Licencia

Creative Commons BY 4.0

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dbGaP phs001245 Autosomal Recessive CD70 Deficiency

Eligibility Criteria

Inclusion and exclusion criteria
Descripción

Inclusion and exclusion criteria

Alias
UMLS CUI [1,1]
C1512693
UMLS CUI [1,2]
C0680251
Patient samples were chosen for inclusion in the project based on the following criteria:
Descripción

Patient samples were chosen for inclusion in the project based on the following criteria:

Tipo de datos

boolean

Alias
UMLS CUI [1,1]
C1512693
UMLS CUI [1,2]
C0370003
Families who had similar syndromic features were studied
Descripción

Families who had similar syndromic features were studied

Tipo de datos

boolean

Alias
UMLS CUI [1,1]
C0015576
UMLS CUI [1,2]
C5453017
UMLS CUI [1,3]
C2348519
Patients, parents and other family members are available
Descripción

Patients, parents and other family members are available

Tipo de datos

boolean

Alias
UMLS CUI [1,1]
C0470187
UMLS CUI [1,2]
C0030705
UMLS CUI [1,3]
C0030551
UMLS CUI [1,4]
C0086282
DNA was available for use in whole genome or exome sequencing
Descripción

DNA was available for use in whole genome or exome sequencing

Tipo de datos

boolean

Alias
UMLS CUI [1,1]
C0470187
UMLS CUI [1,2]
C0012854
UMLS CUI [1,3]
C3640076
UMLS CUI [1,4]
C5575842
Informed consent documentation
Descripción

Informed consent documentation

Tipo de datos

boolean

Alias
UMLS CUI [1,1]
C0021430
UMLS CUI [1,2]
C0920316

Similar models

Eligibility Criteria

Name
Tipo
Description | Question | Decode (Coded Value)
Tipo de datos
Alias
Item Group
Inclusion and exclusion criteria
C1512693 (UMLS CUI [1,1])
C0680251 (UMLS CUI [1,2])
Patient samples were chosen for inclusion in the project based on the following criteria:
Item
Patient samples were chosen for inclusion in the project based on the following criteria:
boolean
C1512693 (UMLS CUI [1,1])
C0370003 (UMLS CUI [1,2])
Families who had similar syndromic features were studied
Item
Families who had similar syndromic features were studied
boolean
C0015576 (UMLS CUI [1,1])
C5453017 (UMLS CUI [1,2])
C2348519 (UMLS CUI [1,3])
Patients, parents and other family members are available
Item
Patients, parents and other family members are available
boolean
C0470187 (UMLS CUI [1,1])
C0030705 (UMLS CUI [1,2])
C0030551 (UMLS CUI [1,3])
C0086282 (UMLS CUI [1,4])
DNA was available for use in whole genome or exome sequencing
Item
DNA was available for use in whole genome or exome sequencing
boolean
C0470187 (UMLS CUI [1,1])
C0012854 (UMLS CUI [1,2])
C3640076 (UMLS CUI [1,3])
C5575842 (UMLS CUI [1,4])
Informed consent documentation
Item
Informed consent documentation
boolean
C0021430 (UMLS CUI [1,1])
C0920316 (UMLS CUI [1,2])

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