ID

45473

Descripción

Principal Investigator: Laura Pasqualucci, MD, Institute for Cancer Genetics, Columbia University, New York, NY, USA MeSH: Lymphoma, Non-Hodgkin,Lymphoma, B-Cell https://www.ncbi.nlm.nih.gov/projects/gap/cgi-bin/study.cgi?study_id=phs000502 Splenic Marginal Zone Lymphoma (SMZL) is a B-cell malignancy of unknown pathogenesis and thus orphan of targeted therapies. By integrating whole-exome sequencing and copy-number analysis of 8 paired tumor-normal DNAs from patients with SMZL, we show that the typical SMZL exome carries ~30 genetic alterations. Targeted resequencing of selected candidates in an extended panel of 40-117 samples revealed activating mutations of NOTCH2, a gene required for marginal-zone (MZ) development, as the most frequent and SMZL-specific lesion, accounting for approximately 20% of cases. Additional altered genes suggest that deregulation of signaling pathways normally involved in MZ development (NOTCH, NF-kappa B, and B-cell receptor) represents a critical event in SMZL pathogenesis. These findings have direct implications for the treatment of SMZL patients since drugs are available which can target NOTCH as well as other pathways deregulated in this disease.

Link

dbGap study = phs000502

Palabras clave

  1. 31/10/22 31/10/22 - Tabea Kampen
  2. 13/12/22 13/12/22 - Kristina Keller
Titular de derechos de autor

Laura Pasqualucci, MD, Institute for Cancer Genetics, Columbia University, New York, NY, USA

Subido en

13 de diciembre de 2022

DOI

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Licencia

Creative Commons BY 4.0

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dbGaP phs000502 Genome-Wide Analysis of Splenic Marginal Zone Lymphoma

Eligibility Criteria

Inclusion and exclusion criteria
Descripción

Inclusion and exclusion criteria

Previously untreated, de novo diagnoses of Splenic Marginal Zone Lymphoma
Descripción

Elig.phs000502.v1.p1.1

Tipo de datos

boolean

Alias
UMLS CUI [1,1]
C0205156
UMLS CUI [1,2]
C0332155
UMLS CUI [1,3]
C1515568
UMLS CUI [1,4]
C0349632
Matched tumor and normal genomic DNA
Descripción

Elig.phs000502.v1.p1.2

Tipo de datos

boolean

Alias
UMLS CUI [1,1]
C0006826
UMLS CUI [1,2]
C0150103
UMLS CUI [2,1]
C0205307
UMLS CUI [2,2]
C0017428
UMLS CUI [2,3]
C0012854

Similar models

Eligibility Criteria

Name
Tipo
Description | Question | Decode (Coded Value)
Tipo de datos
Alias
Item Group
Inclusion and exclusion criteria
Elig.phs000502.v1.p1.1
Item
Previously untreated, de novo diagnoses of Splenic Marginal Zone Lymphoma
boolean
C0205156 (UMLS CUI [1,1])
C0332155 (UMLS CUI [1,2])
C1515568 (UMLS CUI [1,3])
C0349632 (UMLS CUI [1,4])
Elig.phs000502.v1.p1.2
Item
Matched tumor and normal genomic DNA
boolean
C0006826 (UMLS CUI [1,1])
C0150103 (UMLS CUI [1,2])
C0205307 (UMLS CUI [2,1])
C0017428 (UMLS CUI [2,2])
C0012854 (UMLS CUI [2,3])

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