ID

45298

Descrição

Principal Investigator: Christopher A. Walsh, Boston Children's Hospital, Division of Genetics and Genomics, Boston, MA, USA MeSH: Microcephaly,Polymicrogyria,Polymicrogyria, bilateral perisylvian,Pachygyria, frontotemporal,Bilateral periventricular nodular heterotopia,Familial Nodular Heterotopia,Cobblestone lissencephaly,Cerebellar Ataxia,Agenesis of corpus callosum,Epilepsy, Familial Tonic Clonic,Intellectual disability,Abnormalities, Congenital, Nervous System,Dysmorphism Multiple Structural Anomalies,Microcephaly-Micromelia Syndrome,Perisylvian Syndrome https://www.ncbi.nlm.nih.gov/projects/gap/cgi-bin/study.cgi?study_id=phs000492 Developmental brain malformations are at the core of significant neurological diseases affecting many families in the United States and around the world. It is known that epilepsy, specific learning deficits and intellectual disability, cerebral palsy, and abnormalities of brain volume can be attributed in many cases to pathological malformations of the cerebral cortex. Although these consequences, such as epilepsy and intellectual disability, might appear broadly in the population as due to complex traits, this study's focus on those associated with cortical malformations highlights individual developmental pathways likely represented by innumerable and rare Mendelian alleles. Research has thus far uncovered dozens of genes responsible for these conditions and dissected the mechanisms underlying early cortical development in animals. However, this progress represents only the dawn of understanding the complex genetic network and neuronal architecture of the uniquely human cerebral cortex. The overall goal of this study is to define the genetic bases of human cerebral cortical development. This is accomplished through (1) the ascertainment of families with disorders of human brain development and malformation, (2) categorizing these using medical, physical and neuroimaging data, and (3) mapping and identifying the gene causing the disorder of cortical development, which can then be investigated for its normal expression and function, and role in human disease.

Link

dbGaP-study=phs000492

Palavras-chave

  1. 15/10/2022 15/10/2022 - Chiara Middel
  2. 17/10/2022 17/10/2022 - Dr. Christian Niklas
Titular dos direitos

Christopher A. Walsh, Boston Children's Hospital, Division of Genetics and Genomics, Boston, MA, USA

Transferido a

17 octobre 2022

DOI

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Licença

Creative Commons BY 4.0

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dbGaP phs000492 Genetics of Human Developmental Brain Disorders

Eligibility Criteria

Inclusion and exclusion criteria
Descrição

Inclusion and exclusion criteria

Inclusion Criteria: Persons having a brain malformation (i.e.: microcephaly, heterotopias, polymicrogyria, or lissencephaly), familial intellectual disability, and/or epilepsy. Unaffected family members of enrolled probands may also be included. Males and females of any age, race or ethnicity are included.
Descrição

Elig.phs000492.v3.p2.1

Tipo de dados

boolean

Alias
UMLS CUI [1,1]
C1512693
UMLS CUI [1,2]
C0266449
UMLS CUI [1,3]
C0851352
UMLS CUI [1,4]
C3714756
UMLS CUI [1,5]
C0014544
UMLS CUI [2,1]
C1512693
UMLS CUI [2,2]
C0086282
UMLS CUI [2,3]
C0522477
UMLS CUI [3,1]
C1512693
UMLS CUI [3,2]
C3641650
UMLS CUI [3,3]
C0079399
UMLS CUI [3,4]
C0001779
UMLS CUI [3,5]
C0034510
UMLS CUI [3,6]
C0015031
Exclusion Criteria: Persons with a probable non-genetic cause already identified for their brain malformation or intellectual disability, and those without a brain malformation or intellectual disability.
Descrição

Elig.phs000492.v3.p2.2

Tipo de dados

boolean

Alias
UMLS CUI [1,1]
C0680251
UMLS CUI [1,2]
C0332148
UMLS CUI [1,3]
C1298908
UMLS CUI [1,4]
C0019247
UMLS CUI [1,5]
C1314792
UMLS CUI [2,1]
C0680251
UMLS CUI [2,2]
C1298908
UMLS CUI [2,3]
C0266449
UMLS CUI [2,4]
C3714756

Similar models

Eligibility Criteria

Name
Tipo
Description | Question | Decode (Coded Value)
Tipo de dados
Alias
Item Group
Inclusion and exclusion criteria
Elig.phs000492.v3.p2.1
Item
Inclusion Criteria: Persons having a brain malformation (i.e.: microcephaly, heterotopias, polymicrogyria, or lissencephaly), familial intellectual disability, and/or epilepsy. Unaffected family members of enrolled probands may also be included. Males and females of any age, race or ethnicity are included.
boolean
C1512693 (UMLS CUI [1,1])
C0266449 (UMLS CUI [1,2])
C0851352 (UMLS CUI [1,3])
C3714756 (UMLS CUI [1,4])
C0014544 (UMLS CUI [1,5])
C1512693 (UMLS CUI [2,1])
C0086282 (UMLS CUI [2,2])
C0522477 (UMLS CUI [2,3])
C1512693 (UMLS CUI [3,1])
C3641650 (UMLS CUI [3,2])
C0079399 (UMLS CUI [3,3])
C0001779 (UMLS CUI [3,4])
C0034510 (UMLS CUI [3,5])
C0015031 (UMLS CUI [3,6])
Elig.phs000492.v3.p2.2
Item
Exclusion Criteria: Persons with a probable non-genetic cause already identified for their brain malformation or intellectual disability, and those without a brain malformation or intellectual disability.
boolean
C0680251 (UMLS CUI [1,1])
C0332148 (UMLS CUI [1,2])
C1298908 (UMLS CUI [1,3])
C0019247 (UMLS CUI [1,4])
C1314792 (UMLS CUI [1,5])
C0680251 (UMLS CUI [2,1])
C1298908 (UMLS CUI [2,2])
C0266449 (UMLS CUI [2,3])
C3714756 (UMLS CUI [2,4])

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