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ID

45257

Description

Principal Investigator: James J. Goedert, M.D., National Institutes of Health, Bethesda, MD, USA MeSH: HIV,Hemophilia A https://www.ncbi.nlm.nih.gov/projects/gap/cgi-bin/study.cgi?study_id=phs000445 Rare individuals are highly resistant to infection with human immunodeficiency virus (HIV). Studies of candidate genes resulted in the discovery of a 32bp deletion in the CC-chemokine receptor 5 gene (CCR5Δ32), which rendered this critical co-receptor for primary HIV infection to be non-functional. Pharmacologic and vaccine-induced blockade of CCR5 is being pursued to treat and prevent HIV infection and other conditions. The allele frequency of CCR5Δ32 among persons of European ancestry is approximately 10%. CCR5Δ32/Δ32 homozygotes are almost totally resistant to HIV infection. People with severe hemophilia A require frequent replacement with clotting Factor VIII (FVIII) to control hemorrhage. Prior to the discovery of HIV in 1984 and licensure of recombinant FVIII in the late 1980s, people with severe hemophilia A were treated with plasma-derived FVIII and thus were intensively exposed to HIV. Only 5% of such patients were not infected with HIV. Of these, approximately 1/3 were CCR5Δ32/Δ32 homozygotes. The remaining 2/3 of these people who were highly resistant to HIV remain unexplained. This project seeks to discover genome variations among people who are highly resistant to HIV infection. Such variation is likely to serve as a target for reducing the morbidity and incidence of HIV.

Link

dbGaP study = phs000445

Keywords

  1. 6/29/22 6/29/22 - Dr. Christian Niklas
  2. 10/12/22 10/12/22 - Adrian Schulz
Copyright Holder

James J. Goedert, M.D., National Institutes of Health, Bethesda, MD, USA

Uploaded on

October 12, 2022

DOI

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License

Creative Commons BY 4.0

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    dbGaP phs000445 HIV-Resistant People with Hemophilia

    Eligibility Criteria

    Inclusion and exclusion criteria
    Description

    Inclusion and exclusion criteria

    The study includes only people with hemophilia who were proven to be uninfected with HIV despite having received plasma-derived clotting factor concentrates that conveyed a 95% likelihood of HIV infection.
    Description

    Elig.phs000445.v1.p1.1

    Data type

    boolean

    Alias
    UMLS CUI [1,1]
    C1512693
    UMLS CUI [1,2]
    C0481430
    UMLS CUI [1,3]
    C0684275
    UMLS CUI [1,4]
    C0199967
    UMLS CUI [1,5]
    C0032105
    UMLS CUI [1,6]
    C0023707
    UMLS CUI [1,7]
    C5392830

    Similar models

    Eligibility Criteria

    Name
    Type
    Description | Question | Decode (Coded Value)
    Data type
    Alias
    Item Group
    Inclusion and exclusion criteria
    Elig.phs000445.v1.p1.1
    Item
    The study includes only people with hemophilia who were proven to be uninfected with HIV despite having received plasma-derived clotting factor concentrates that conveyed a 95% likelihood of HIV infection.
    boolean
    C1512693 (UMLS CUI [1,1])
    C0481430 (UMLS CUI [1,2])
    C0684275 (UMLS CUI [1,3])
    C0199967 (UMLS CUI [1,4])
    C0032105 (UMLS CUI [1,5])
    C0023707 (UMLS CUI [1,6])
    C5392830 (UMLS CUI [1,7])

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