ID

45221

Description

Principal Investigator: Kevin M. Brown, PhD, National Cancer Institute, National Institutes of Health, Bethesda, MD, USA MeSH: Melanoma https://www.ncbi.nlm.nih.gov/projects/gap/cgi-bin/study.cgi?study_id=phs000419 We conducted whole-genome sequencing of probands from several melanoma families, identifying one individual carrying a novel germline variant (c.G1075A, NM_000248.3; p.E318K, NP_000239.1; rs149617956) in the melanoma lineage-specific oncogene MITF. While the variant cosegregated with melanoma in some, but not all cases in the family, linkage analysis of 31 families subsequently identified to carry the variant generated a LOD score of 2.7 under a dominant model, suggesting E318K as a possible intermediate risk variant. Consistent with this, E318K was significantly associated with melanoma in a large Australian case-control sample, giving an odds ratio (OR) of 2.33, 95% CI 1.21-4.70 (case and control carrier frequency, 0.0165 and 0.0072, respectively; P=0.008). Likewise, it was similarly associated in an independent case-control sample from the United Kingdom (UK P=0.012; combined P=0.0003, OR 2.19, 95% CI 1.41-3.45). In the Australian sample, the variant allele was significantly over-represented in cases with a family history of melanoma (OR 2.95, 95% CI 1.23-6.92), multiple primary melanomas (OR 4.22, 95% CI 1.52-10.91), or both (OR 8.37, 95% CI 2.58-23.80). The variant allele was also associated with increased nevus count (combined P=0.002, OR 2.54, 95% CI 1.42-4.55) and non-blue eye color (combined P=0.008, OR 2.01, 95% CI 1.11-3.81). Functional analysis of E318K showed that MITF encoded by the variant allele had impaired sumoylation and differentially regulated several MITF targets. These data indicate that MITF is a melanoma predisposition gene and highlights the utility of whole-genome sequencing to identify novel rare variants associated with disease susceptibility.

Link

dbGaP study = phs000419

Keywords

  1. 7/31/22 7/31/22 - Simon Heim
  2. 10/12/22 10/12/22 - Adrian Schulz
Copyright Holder

Kevin M. Brown, PhD, National Cancer Institute, National Institutes of Health, Bethesda, MD, USA

Uploaded on

October 12, 2022

DOI

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License

Creative Commons BY 4.0

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dbGaP phs000419 A Novel Recurrent Mutation in MITF Predisposes to Familial and Sporadic Melanoma

Eligibility Criteria

Inclusion and exclusion criteria
Description

Inclusion and exclusion criteria

Families sequenced were negative for mutations to CDKN2A and CDK4, and had a minimum of two additional first- or second- degree relatives diagnosed with melanoma.
Description

Families sequenced were negative for mutations to CDKN2A and CDK4, and had a minimum of two additional first- or second- degree relatives diagnosed with melanoma.

Data type

boolean

Alias
UMLS CUI [1,1]
C1706256
UMLS CUI [1,2]
C1512693
UMLS CUI [1,3]
C4699042
UMLS CUI [1,4]
C2736925
UMLS CUI [1,5]
C1517194
UMLS CUI [1,6]
C1519210
UMLS CUI [1,7]
C0522476
UMLS CUI [1,8]
C0025202

Similar models

Eligibility Criteria

Name
Type
Description | Question | Decode (Coded Value)
Data type
Alias
Item Group
Inclusion and exclusion criteria
Families sequenced were negative for mutations to CDKN2A and CDK4, and had a minimum of two additional first- or second- degree relatives diagnosed with melanoma.
Item
Families sequenced were negative for mutations to CDKN2A and CDK4, and had a minimum of two additional first- or second- degree relatives diagnosed with melanoma.
boolean
C1706256 (UMLS CUI [1,1])
C1512693 (UMLS CUI [1,2])
C4699042 (UMLS CUI [1,3])
C2736925 (UMLS CUI [1,4])
C1517194 (UMLS CUI [1,5])
C1519210 (UMLS CUI [1,6])
C0522476 (UMLS CUI [1,7])
C0025202 (UMLS CUI [1,8])

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