ID

45178

Beschrijving

Principal Investigator: Charles Mullighan, MBBS(Hons), MSc, MD, Dept. of Pathology, St. Jude Children's Research Hospital, Memphis, TN, USA MeSH: Precursor Cell Lymphoblastic Leukemia-Lymphoma https://www.ncbi.nlm.nih.gov/projects/gap/cgi-bin/study.cgi?study_id=phs000341 The genetic basis of hypodiploid acute lymphoblastic leukemia (ALL), a subtype of ALL characterized by aneuploidy and poor outcome, is unknown. Genomic profiling of 124 hypodiploid ALL cases, including whole-genome and exome sequencing of 40 cases, identified two subtypes that differ in the severity of aneuploidy, transcriptional profiles and submicroscopic genetic alterations. Near-haploid ALL with 24-31 chromosomes harbor alterations targeting receptor tyrosine kinase signaling and Ras signaling (71%) and the lymphoid transcription factor gene IKZF3 (encoding AIOLOS; 13%). In contrast, low-hypodiploid ALL with 32-39 chromosomes are characterized by alterations in TP53 (91.2%) that are commonly present in nontumor cells, IKZF2 (encoding HELIOS; 53%) and RB1 (41%). Both near-haploid and low-hypodiploid leukemic cells show activation of Ras-signaling and phosphoinositide 3-kinase (PI3K)-signaling pathways and are sensitive to PI3K inhibitors, indicating that these drugs should be explored as a new therapeutic strategy for this aggressive form of leukemia.

Link

dbGaP study = phs000341

Trefwoorden

  1. 22-08-22 22-08-22 - Simon Heim
  2. 12-10-22 12-10-22 - Adrian Schulz
Houder van rechten

Charles Mullighan, MBBS(Hons), MSc, MD, Dept. of Pathology, St. Jude Children's Research Hospital, Memphis, TN, USA

Geüploaded op

12 oktober 2022

DOI

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Licentie

Creative Commons BY 4.0

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dbGaP phs000341 The Genetic Basis of Hypodiploid ALL

Eligibility Criteria

Inclusion and exclusion criteria
Beschrijving

Inclusion and exclusion criteria

Primary pediatric and adult acute lymphoblastic leukemia cases with material available for genome-wide profiling.
Beschrijving

Primary pediatric and adult acute lymphoblastic leukemia cases with material available for genome-wide profiling.

Datatype

boolean

Alias
UMLS CUI [1,1]
C0023449
UMLS CUI [1,2]
C0470187
UMLS CUI [1,3]
C0370003

Similar models

Eligibility Criteria

Name
Type
Description | Question | Decode (Coded Value)
Datatype
Alias
Item Group
Inclusion and exclusion criteria
Primary pediatric and adult acute lymphoblastic leukemia cases with material available for genome-wide profiling.
Item
Primary pediatric and adult acute lymphoblastic leukemia cases with material available for genome-wide profiling.
boolean
C0023449 (UMLS CUI [1,1])
C0470187 (UMLS CUI [1,2])
C0370003 (UMLS CUI [1,3])

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